Medical Science Liaison - Gene Therapy (Eastern US) USA - West
Virginia - Charleston (Remote)
USA - Georgia - Atlanta (Remote)
USA - South Carolina - Columbia (Remote)
USA - Rhode Island - Providence (Remote)
USA - Delaware - Dover (Remote)
USA - Pennsylvania - Philadelphia (Remote)
USA - Connecticut - Hartford (Remote)
USA - New York - New York (Remote)
USA - Mississippi - Jackson (Remote)
USA - Massachusetts - Lynnfield (Remote)
USA - Maryland - Baltimore (Remote)
USA - Maine - Portland (Remote)
Job Description Summary: The Gene Therapy Medical Science
Liaison (GT-MSL) - is a regional position supporting the scientific
and clinical interests of PTC Therapeutics by interacting with
current and future thought leaders in academic, clinical, and
diagnostic medicine at the regional and national level through
fair-balanced scientific and clinical discussions. These thought
leader interactions will complement or supplement the overall Gene
Therapy Medical Affairs program initiatives. The GT-MSL must
possess strong scientific and clinical acumen, have a strong
interest in gene therapy, and a true passion to help bring
innovative medicines to patients with rare diseases. They will be
leading the efforts for our gene therapy launch. The GT-MSL must
possess the capacity to coordinate and manage solo initiatives or
partnerships with external partners independently or with a minimum
amount of oversight. The Medical Science Liaison supports adherence
to relevant regulatory requirements and company Standard Operating
Procedures (SOPs) as appropriate. This position will report into
Head, US Medical Affairs Gene Therapy and work closely with
internal cross functional partners such as Commercial, Market
Access, and Marketing. Job Description: Is the external medical and
scientific face of PTC gene therapy and, as such, is expected to
possess strong scientific and clinical acumen.
Attends national and regional medical meetings and symposia as a
representative of PTC and engages in discussions with attendees as
appropriate; attends scientific sessions and poster presentations,
gathers information, and summarizes findings; as possible, and when
appropriate, cultivates professional relationships from these
Delivers, and may develop/design, fair-balanced and objective
clinical and scientific presentations to healthcare professionals
(HCPs), payors, patient organizations in response to unsolicited
requests for information on the use of company products.
Identifies and trains speakers for advisory boards, symposia,
and educational programs with regulatory approved materials, slides
sets, abstracts, posters, etc.
Identifies, organizes, and facilitates regional medical
initiatives e.g. advisory board as needed.
Provides input to management regarding alternative therapies,
business development opportunities/risks, and client feedback.
Establishes, manages, and maintains successful relations with
relevant health care workers and health institutions, including but
not limited to: KOLs, HCPs, academic institutions, payors, patient
Facilitates the accurate and timely submission of applications
for unrestricted educational grants or research initiatives and
requests for support of studies (IISs), per company policy.
Maintains a thorough awareness of medical/clinical, regulator,
compliance and quality issues and processes as they apply to the
PTC therapeutic areas and adheres to, and supports, the standards
established by the company.
Maintains competitor information relevant to company’s
therapeutic areas, goals/objectives, project activities and
/product team priorities and stays current on therapeutic advances
and competing therapies or products; analyzes and applies relevant
intelligence findings and communicates and presents insightful
data/impact in an efficient format to appropriate internal stake
Qualifications: Advanced degree (e.g. PharmD, M.D. or Ph.D.) in
a scientific discipline and a minimum of 4 years progressively
responsible, relevant experience in a pharmaceutical, biotechnology
or related environment with a minimum of 2 years’ experience as an
* Special knowledge or skills needed and/or licenses or
In-depth, hands-on experience working with KOLs, clinicians,
HCPs, payors, and/or academic institutions establishing/maintaining
relationships with scientific and medical credibility.
Demonstrated success in understanding and interpreting
scientific data. Demonstrated success in presenting research
information to scientists and HCPs. Comfortable presenting
scientific and clinical data to varying audiences.
Excellent understanding of the pharmaceutical delivery
Ability to influence without direct authority.
Proficiency with Microsoft Office.
Excellent verbal and written communication and skills, including
scientific/ technical writing and presentations including the
ability to communicate complex technical information clearly.
Ability to work independently and collaboratively, as required,
in a fast-paced, matrixed, team environment consisting of internal
and external team members.
Analytical thinker with excellent problem-solving skills and the
ability to adapt to changing priorities and deadlines.
Excellent planning, organization and time management skills
including the ability to support and prioritize multiple
Must possess a valid driver’s license and a personal automobile
with an active vehicle insurance policy. Must be able to travel
daily to/from customer accounts and drive and/or fly long distances
(distances will vary based upon the size of assigned
This position requires overnight travel, the amount of which
will vary based upon the assigned territory. In addition to travel
within the territory, overnight and/or weekend travel outside of
the assigned territory is required.
Daily entry to hospitals and other medical facilities is
required. Many facilities have instituted vendor credentialing
policies which require vendors to meet defined training, background
check and proof of immunization requirements as a condition of
entry. PTC employees entering these facilities are required to
abide by these credentialing requirements.
*Special knowledge or skills and/or licenses or certificates
Experience supporting an orphan, rare disease, and/or
Experience with Gene Therapy
* Travel requirements: 70-80%
Territory coverage: (Candidate must live within region)
New England Region: ME, NH, VT, CT, NY, PA, NJ, RI, MA
Atlantic Region: MI, IL, OH, WV, MD, DE, KY, TN, NC, SC, AL, MS,
PTC Therapeutics is an equal opportunity employer. We welcome
applications from all individuals, regardless of race, color,
national origin, gender, age, physical characteristics, social
origin, disability, religion, family status, pregnancy, sexual
orientation, gender identity, gender expression, disability,
veteran status or any unlawful criterion under applicable law. We
are committed to treating all applicants fairly and avoiding
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PTC is biopharmaceutical company focused on the discovery and
development of orally-administered, proprietary small molecule
drugs that target post-transcriptional control processes. While
PTC’s discovery programs are directed at targets in multiple
therapeutic areas, PTC is focusing particularly on the development
and commercialization of treatments for orphan and ultra-orphan
disorders. Post-transcriptional control processes regulate the rate
and timing of protein production and are essential to proper
cellular function. PTC’s internally-discovered pipeline addresses
multiple therapeutic areas, including neuromuscular disorders,
oncology and infectious diseases. For more information on the
company, please visit our website www.ptcbio.com. ?